Muscular dystrophy is a complex condition that impacts the function of the muscles. There are many forms of this genetic disorder, and treatment approaches vary based on this and other factors. Despite these variations, medication often plays a role in muscular dystrophy treatment, as certain drugs can have a positive impact on symptoms.
Because muscular dystrophy cannot be cured, doctors focus on managing its symptoms and improving quality of life for patients. When it comes to medication, corticosteroids slow down the progression of muscle weakness and atrophy. These drugs can also increase a person’s lifespan by preventing lung and heart dysfunction.
For people with myotonic dystrophy, which causes muscle spasms, muscle relaxants can help. In the event that heart problems have already occurred, heart medications like beta blockers and ACE inhibitors will be prescribed.
Duchenne muscular dystrophy (DMD) is the most common form of the disorder and can impact the function of the heart and lungs as it progresses. However, medical research has led to new medications that can significantly alter the course of the disorder and prevent people with it from experiencing major health effects.
One medication called eteplirsen works by making up for a lack of a protein called dystrophin, which is instrumental in the function of muscles throughout the body. Studies show that the medication reduced hospitalization and improved both lung and heart function in study participants. While research continues into this disorder, these advances show immense promise for people living with muscular dystrophy.